Neuromuscular

Clinical Research


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If you think you may qualify for one of these studies, please contact Neurology Research Partners at (303) 724-4644 or NeurologyResearchPartners@CUAnschutz.edu

 

 

COMIRB #Title (Please click on the title to see approved advertisement)Principal InvestigatorEligibility and InformationAdvertisement
Amyotrophic Lateral Sclerosis    
19-1560

Radicava/Edaravone Findings in Biomarkers From ALS (REFINE-ALS)

Laura Foster, MDClinical TrialsN/A
19-2645Healey ALS Platform TrialLaura Foster, MDClinical TrialsPlatform Video
Chronic Inflammatory Demyelinating Polyneuropathy    
19-1455Phase III Efficacy, Safety, and Tolerability Study of HYQVIA/HyQvia and GAMMAGARD LIQUID/KIOVIG
in CIDP
Matthew Wicklund, MDClinical TrialsN/A

Charcot Marie Tooth Disease

    
18-2537Natural History Evaluation of Charcot Marie Tooth Disease (CMT) Types CMT1B, CMT2A, CMT4A, CMT4C, and Others (INC-6601)Vera Fridman, MDClinical TrialsN/A
20-1525Genetics of CMT – Modifiers of CMT1A, New Causes of CMT (INC-6602)Vera Fridman, MDClinical TrialsN/A

Facioscapulohumeral Muscular Dystrophy

    
20-0405Motor Outcomes to Validate Evaluations in FSHD (MOVE FSHD)Matthew Wicklund, MDClinical TrialsN/A
Inclusion Body Myositis    
17-1132Using Next Generation Sequencing to Unravel the Pathogenesis of Sporadic Inclusion Body Myositis (IBM) – The International IBM Consortium Genetic StudyMatthew Wicklund, MDClinical TrialsN/A
Limb Girdle Muscular Dystrophy    
19-2943Biomarker Development in LGMD 2i (MLB-01-001) Matthew Wicklund, MDClinical TrialsN/A
19-0506Defining Clinical Endpoints in Limb Girdle Muscular Dystrophy (LGMD) (GRASP)Matthew Wicklund, MDClinical TrialsN/A
Myasthenia Gravis    
19-1597A Study to Test Efficacy and Safety of Rozanolixizumab in Adult Patients with Generalized Myasthenia GravisStacy Dixon, MD, PhDClinical TrialsN/A
20-0609A Study of TAK-079 in People with Generalized Myasthenia GravisThomas Ragole, MDClinical TrialsN/A
20-1787

Myasthenia Gravis Inebilizumab Trial (MINT)

Dianna Quan, MDClinical TrialsN/A
TTR Amyloidosis    
08-0623Transthyretin-Associated Amyloidoses Outcomes Survey (THAOS): A Global, Multi-Center, Longitudinal, Observational Survey of Patients with Documented Transthyretin (TTR) Mutations or Wild-Type TTR AmyloidosisDianna Quan, MDClinical TrialsN/A
19-2873NEURO-TTRansform: A Study to Evaluate the Efficacy and Safety of AKCEA-TTR-LRx in Participants With Hereditary Transthyretin-Mediated Amyloid PolyneuropathyDianna Quan, MDClinical TrialsN/A